"This is the part worth pausing on, because it inverts the usual assumption about rare disease. The conventional view treats ultra-rare conditions as charity cases - worthy, tragic, and commercially hopeless. Grace Science's wager is the opposite: that a rare disease is a keyhole."
A father couldn't find a treatment for his daughter's ultra-rare disease. So he co-founded a biotech with a Nobel laureate. Full story on https://yespress.io/grace-science-llc?utm_source=bluesky&utm_medium=social