Glycocalyx-edited mesenchymal stem/stromal cell therapy in advanced osteoporosis: Cell www.cell.com/cell/fulltex...

Glycocalyx-edited mesenchymal stem/stromal cell therapy in advanced osteoporosis

Mesenchymal stem/stromal cell (MSC)-based therapy holds promise for reversal of bone loss in osteoporosis. This phase 1 study establishes the safety and feasibility of intravenous administration of gl...

cell.com

Congratulations to all #Huntingtonsdisease advocates who have fought hard for this. Best of luck UniQure. 💙💜

STAT@statnews.com · 3mo ago

The FDA has reversed its opposition to UniQure's closely watched experimental treatment for Huntington’s disease, clearing a path for the company to file for U.S. approval. UniQure will submit a marketing application in Q3 seeking accelerated approval.

F.D.A. Commissioner Marty Makary Resigns After Weeks of Pressure www.nytimes.com/2026/05/12/u...

F.D.A. Commissioner Marty Makary Resigns After Weeks of Pressure

nytimes.com

Biotech raises $42 million to run #Huntingtonsdisease trial www.statnews.com/2026/05/04/b... via @statnews.com

Biotech raises $42 million to run Huntington’s disease trial

Latus Bio raised $42 million as it prepares to seek FDA approval to start a clinical trial for its gene therapy for Huntington's disease.

statnews.com

This is a bit late, but I wanted to give Dr. Wendy Campana a shout out because she’s awesome and we are so glad she came to UCDavis! @ucdavis.bsky.social

Department of Cell Biology and Human Anatomy@ucd-cbha.bsky.social · 6mo ago

We have a new fearless leader! Welcome Dr. Wendy Campana: health.ucdavis.edu/news/headlin...

Honored to be part of this trial, led by my amazing colleague Dr. Farmer, with much teamwork. Thank you for funding from @cirmnews.bsky.social (CIRM). 🫶 Treating fetuses with stem cells proves safe in milestone spina bifida trial | Science | AAAS www.science.org/content/arti...

Treating fetuses with stem cells proves safe in milestone spina bifida trial

The study is now scaling up to do more in utero procedures and evaluate effects on disability as children grow

science.org

She Was Born Without an Immune System. Gene Therapy Saved Her Life. www.nytimes.com/2025/11/27/w...

She Was Born Without an Immune System. Gene Therapy Saved Her Life.

nytimes.com

Congratulations to Capricor, PI Dr. Craig McDonald of @ucdavishealth.bsky.social & the patients for these exciting results. Thank you to our @cirmnews.bsky.social - funded Alpha Clinic for assisting with the trial logistics & product formulation and delivery. 🙏 www.capricor.com/investors/ne...

Capricor Therapeutics Announces Positive Topline Results from Pivotal Phase 3 HOPE-3 Study of Deramiocel in Duchenne Muscular Dystrophy

Pivotal Phase 3 randomized, double-blind, placebo-controlled study (n=106) met the primary endpoint (PUL v2.0) and the key secondary cardiac…...

capricor.com

Thank you Judge Lin! “As a part of Friday’s ruling, Judge Lin said the defendants in the case, including Mr. Trump and an array of government agencies, could not link federal funding “to any measures” that would violate the First Amendment.” www.nytimes.com/2025/11/14/u...

Judge Orders Trump Not to Threaten University of California’s Funding

nytimes.com

Baby KJ; doctors will ask FDA this winter to OK a clinical trial of pioneering gene editing approach. #genetherapy #baseediting #crispr #geneediting www.statnews.com/2025/10/16/b... via @statnews.com

Baby KJ's doctors will ask FDA this winter to OK a clinical trial of pioneering gene editing approach

Baby KJ's medical team intend to ask the FDA to start a clinical trial that would be open to patients with seven different urea cycle disorders.

statnews.com

#NORDSummit: Lee Greenwood, whose 5-year-old daughter Noa was born with #CanavanDisease, a severe #GeneticDisorder found mainly among Ashkenazi Jews. In June 2022, the girl received lifesaving #GeneTherapy and is now developing normally. @nordrare.bsky.social #RareDisease #RareSky #MedSky

A new review highlights the advances in DNA nucleases and delivery vectors for in vivo #GeneTherapy, outlining key developments, challenges, and their future potential to treat diverse #Diseases. #medsky #OpenAccess: www.sciencedirect.com/science/arti...

This Month on HemeHub: SCD and Gene Therapy Join us as we explore advances in the treatment of #sicklecelldisease through #genetherapy, featuring pivotal trials of Lyfgenia and Casgevy. Stay tuned for our upcoming session featuring Dr. John Tisdale, Senior Investigator at the NHLBI.

basicscience.ucdmc.ucdavis.edu/beleford-lab...

Congratulations to ⁦‪UniQure and to the #huntingtonsdisease community! 💙💜 www.uniqure.com/investors-me...

Press Releases | Investors & Media

Reimagining the future of healthcare through the power of gene therapy.

uniqure.com

AABB’s Cell and Gene Therapy Standards for Pharmacy, First Edition, Takes Effect October 1 - bioinformant.com/aabbs-cell-a... @aabbupdates.bsky.social

AABB’s Cell and Gene Therapy Standards for Pharmacy, First Edition, Takes Effect October 1 | BioInformant

Sept 8, 2025, Bethesda, MD – The Association for the Advancement of Blood & Biotherapies (AABB) is pleased to announce the release of the first edition of Cell and Gene Therapy Standards for Pharmacy,...

bioinformant.com

Congratulations to Brian Fury, our GMP Facility Director at UC Davis Health @ucdavis.bsky.social, and to all of the other recipients of these G-Rex grant awards from ScaleReady. www.prnewswire.com/news-release...

ScaleReady Awards G-Rex® Grants to Support Cell and Gene Therapy Manufacturing in California

/PRNewswire/ -- ScaleReady, in collaboration with Wilson Wolf Manufacturing, Bio-Techne Corporation (NASDAQ: TECH) and CellReady, today announced that eight...

prnewswire.com

UC Davis & @ucsanfrancisco.bsky.social scientists completed a clinical trial on a new cancer drug for pet cats with squamous cell carcinoma. Researchers believe it will also be effective for humans with similar head and neck cancers. Read more about the clinical trial: ucdav.is/46dxcfM

Momentary break for a much-needed palate cleanser. 🫠 Never knew these adorable creatures existed until this moment. (and nope, it is not AI- they are real! 🥰)

Cephalopods Daily@cephalopodsdaily.bsky.social · last yr.

Piglet squids (genus Helicocranchia) are a genus of small cranchiids known for their goofy appearance. They have a rather large siphon that make them look like a pig with a snout. Well I guess with their arms raised up cranchiid style, they look like a pig with a crazy hairdo. #SQUIDtember

I am so honored to be a part of this team. Thank you to the NIH for starting up their funding again. Please hang in there, fellow scientists! health.ucdavis.edu/medical-scho...

Dream team to develop in utero gene editing therapy for a rare neurological genetic disorder

Professor Aijun Wang won a $3.2 million NIH grant to develop a cure to Dup15q syndrome using an in-utero gene editing formula.

health.ucdavis.edu

🚨 NEW PUBLICATION 🚨 "Human brain vascular multi-omics elucidates disease-risk associations" www.cell.com/neuron/abstr... @ucsanfrancisco.bsky.social @madiganreid.bsky.social @cellpress.bsky.social

Human brain vascular multi-omics elucidates disease-risk associations

Reid et al. develop MultiVINE-seq to map thousands of non-coding disease variants to genes in human brain vascular cells. Cerebrovascular disease variants compromise vessel integrity, whereas Alzheime...

cell.com

Want to collaborate with the International Brain Laboratory on your own project? We have funding to work with groups anywhere in the world to do new large-scale projects and we are looking for new partners! Learn more and apply: www.internationalbrainlab.com/ibl-core-apply

House appropriators snub Kennedy, include mRNA vaccine funding in spending bill www.statnews.com/2025/09/10/m... via @statnews.com

House appropriators snub Kennedy, include mRNA vaccine funding in spending bill

Lawmakers have snubbed health secretary RFK Jr. by including an amendment in a spending bill mandating that an agency under his purview continue to research messenger RNA vaccines.

statnews.com

The regime halted all federal grants then told UC administration if they pay $1 billion they could have them back. It’s like ransomware. UC is a public university system and we cannot do this. So, no grants = no research and labs will shut down. Are we great yet? dailybruin.com/2025/08/09/a...

'An attack on knowledge': UCLA researchers say lifesaving research is in jeopardy - Daily Bruin

Dr. Jerzy Kupiec-Weglinski has led organ transplant research at UCLA for nearly three decades. Kupiec-Weglinski, the vice chairman of basic science research in the David Geffen School of Medicine’s su...

dailybruin.com

The regime halted all federal grants then told UC administration if they pay $1 billion they could have them back. It’s like ransomware. UC is a public university system and we cannot do this. So, no grants = no research and labs will shut down. Are we great yet? dailybruin.com/2025/08/09/a...

'An attack on knowledge': UCLA researchers say lifesaving research is in jeopardy - Daily Bruin

Dr. Jerzy Kupiec-Weglinski has led organ transplant research at UCLA for nearly three decades. Kupiec-Weglinski, the vice chairman of basic science research in the David Geffen School of Medicine’s su...

dailybruin.com

Trump administration violated impoundment law by canceling NIH grants, slowing new awards, GAO finds www.statnews.com/2025/08/05/g... via @statnews.com

Trump administration violated impoundment law by canceling NIH grants, slowing new awards, GAO finds

The Government Accountability Office found that the Trump administration, by abruptly canceling NIH grants, had violated a 1974 federal law

statnews.com

Good morning and happy Saturday. Take a deep breath and keep riding those waves. 🙏

Stimulating immune cells in vitro is a common experimental lab model. We profiled 150K blood immune cells treated with 11 different stimuli to compare the effects. The data are freely available for researchers. See the preprint for our findings and to access the data 🧪 doi.org/10.1101/2025...

Bioengineered immunocompetent preclinical trial-on-chip tool enables screening of CAR T cell therapy for leukaemia. #Tcell #immunotherapy #organonachip 🧪https://www.nature.com/articles/s41551-025-01428-2

Bioengineered immunocompetent preclinical trial-on-chip tool enables screening of CAR T cell therapy for leukaemia - Nature Biomedical Engineering

An ex vivo organotypic and immunocompetent human leukaemia chip system is used for CAR T cell therapy modelling and screening of patient response.

nature.com

After spearheading a 34% cut in cancer mortality, the National Cancer Institute at the NIH is bleeding resources and staff and could see its budget cut by nearly 40%. kffhealthnews.org/news/article...

World’s Premier Cancer Institute Faces Crippling Cuts and Chaos - KFF Health News

After spearheading a 34% cut in cancer mortality, the National Cancer Institute at the NIH is bleeding resources and staff and could see its budget cut by nearly 40%.

kffhealthnews.org