Revolutionary findings show LEAPER 2.0 achieves long-term exon skipping in DMD, using circ-arRNAs for muscle regeneration in monkeys and humans. Exciting progress! PMID:42269605, Cell 2026, @Cell https://www.cell.com/cell/fulltext/S0092-8674(26)00589-1 #Medsky #Pharmsky #RNA #ASHG #ESHG 🧪
https://www.cell.com/cell/fulltext/S0092-8674(26)00589-1
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